Niemann-Pick Disease

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What is Niemann-Pick Disease?

Niemann-Pick disease is an inherited condition involving lipid metabolism, which is the breakdown, transport, and use of fats and cholesterol in the body. Symptoms are related to the organs in which lipids accumulate.

What is it like to have Niemann-Pick Disease?


Reports may be affected by other conditions and/or medication side effects. We ask about general symptoms (anxious mood, depressed mood, insomnia, fatigue, and pain) regardless of condition.
Last updated:

What do patients take to treat Niemann-Pick Disease and its symptoms?

You’ve tried
Treatment name(s)
Type
How many have tried
How many evaluations
Type
Prescription Drug
How many have tried
1
How many evaluations
2

Data from patients with Niemann-Pick Disease, who reported starting treatments within the last 5 years.
Last updated:
You’ve tried this treatment.

Compare treatments for Niemann-Pick Disease

You’ve tried
Treatment name(s)
How many have tried
Perceived effectiveness
Side effects
How many evaluations
How many have tried
1
Perceived effectiveness
Side effects
How many evaluations
2

Data from patients with Niemann-Pick Disease, who reported starting treatments within the last 5 years.
Last updated:
You’ve tried this treatment.

  • Major
  • Moderate
  • Slight
  • None
  • Can't tell
  • Severe
  • Moderate
  • Mild
  • None

Who has Niemann-Pick Disease on PatientsLikeMe?


Age
Age Proportion # of patients
<20 12
20s 3
30s 3
40s 1
50s 0
60s 1
70+ 0

Gender

Distribution of females vs. males

41% Females
59% Males
Age at first symptom
Age at first symptom Proportion # of patients
0-19 years 9
20-29 years 1
30-39 years 0
40-49 years 0
50-59 years 0
60-69 years 0
70+ years 0

Types
Condition Types Proportion # of patients
Type A 0
Type B 0
Type C 7
Type D 0
Type E 0
Diagnosis status
Diagnosis status Proportion # of patients
Diagnosed 16
Not Diagnosed 0

These charts show data from NPD patients who have completed their condition history
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